The FDA has granted an accelerated approval for Otarmeni (lunsotogene parvec-cwha), the first gene therapy to treat patients with biallelic variants in the OTOF gene. The gene therapy will be made available to eligible patients at no cost, according to a news release from Regeneron, the therapy’s developer.

A novel strategy that combines computational and experimental approaches has allowed researchers at Baylor College of Medicine and the Duncan Neurological Research Institute (Duncan NRI) at Texas Children's Hospital to distinguish alterations in gene function that contribute to Parkinson's disease from those that protect from the condition.

A new study finds that bacteria can actively block the transfer of beneficial genes to neighboring cells, using specialized proteins to specifically destroy shared DNA before it spreads. This challenges the long-held view that bacteria freely exchange genetic material and reveals a more competitive system in which microbes tightly control who gets access to valuable traits,

Molecular biologist Jean Bennett and ophthalmologist Albert Maguire were awarded the $3 million Breakthrough Prize in Life Sciences alongside physician Katherine High for developi

Researchers have discovered that some bacteria use a protein called YokF to actively block plasmid DNA transfer through nanotubes, preventing neighboring cells from acquiring potentially beneficial traits like antibiotic resistance. The study, published in ...

Chicken eggs are already used to harvest helpful proteins called antibodies to protect humans from viruses such as influenza. Now, a breakthrough at the University of Missouri could one day lead to chickens that produce other useful medical proteins in their eggs.

The skin over a fresh wound might not look like much. In some animals, though, that thin covering becomes command central for rebuilding what was lost.

Saffie's mum says Luxturna therapy at Great Ormond Street has been like "someone waved a magic wand".